For Patients

X4’s mission is to bring innovative treatments to patients with rare diseases, including primary immunodeficiencies and cancer. To fulfill this mission, we seek to maintain a sense of urgency and commitment to rigorous science and the highest integrity in drug development. We engage with the health care community to help ensure that we align with its highest needs and strive to make a profound and positive impact on the lives of patients and their families.

We invite you to learn more about us and our efforts to deliver new treatments for rare diseases, including primary immunodeficiencies and cancer through the information and references outlined in this section.

Paula Ragan, PhD
Founder and CEO, X4 Pharmaceuticals